{"id":145644,"date":"2022-09-02T01:33:59","date_gmt":"2022-09-02T01:33:59","guid":{"rendered":"https:\/\/labinsights.com\/acf_article\/%e6%96%b0%e5%85%b4%e8%a1%80%e5%8f%8b%e7%97%85%e7%96%97%e6%b3%95%e5%87%b8%e6%98%be%e9%ab%98%e8%b4%a8%e9%87%8f%e8%af%8a%e6%96%ad%e9%9c%80%e6%b1%82\/"},"modified":"2026-03-04T10:14:44","modified_gmt":"2026-03-04T10:14:44","slug":"emerging-haemophilia-therapies-highlight-a-need-for-quality-diagnostics","status":"publish","type":"acf_article","link":"https:\/\/labinsights.com\/zhcn\/disease-area\/rare-diseases\/emerging-haemophilia-therapies-highlight-a-need-for-quality-diagnostics\/","title":{"rendered":"\u65b0\u5174\u8840\u53cb\u75c5\u7597\u6cd5\u51f8\u663e\u9ad8\u8d28\u91cf\u8bca\u65ad\u9700\u6c42"},"content":{"rendered":"

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[1]<\/a> \u7f8e\u56fd\u75be\u75c5\u63a7\u5236\u4e0e\u9884\u9632\u4e2d\u5fc3\uff0c\u8840\u53cb\u75c5\u4e3b\u9875-\u6291\u5236\u5242\u4e0e\u8840\u53cb\u75c5 https:\/\/www.cdc.gov\/ncbddd\/hemophilia\/inhibitors.html [2] Mannucci, P., 2020.<\/p>\n

[2]<\/a> Mannucci, P., 2020. Hemophilia therapy: the future has begun.Haematologica, 105(3), pp.545-553.<\/p>\n

[3]<\/a> FDA approves emicizumab-kxwh for prevention and reduction of bleeding in patients with hemophilia A with factor VIII inhibitors. https:\/\/www.fda.gov\/drugs\/resources-information-approved-drugs\/fda-approves-emicizumab-kxwh-prevention-and-reduction-bleeding-patients-hemophilia-factor-viii<\/p>\n

[4]<\/a> CSL Behring gene therapy makes comeback after hold for FDA priority review. https:\/\/www.fiercebiotech.com\/biotech\/2020-trial-pause-isnt-holding-csl-behring-back-fda-oks-priority-review-application<\/p>\n

[5]<\/a> BioMarin\u2019s haemophilia gene therapy Roctavian wins conditional EU backing amid FDA delay. https:\/\/www.fiercepharma.com\/pharma\/biomarins-hemophilia-gene-therapy-roctavian-wins-conditional-eu-backing-fda-plan-delayed<\/p>\n

[6] <\/a>World Federation of Haemophilia Guidelines for the Management of Haemophilia. https:\/\/www1.wfh.org\/publications\/files\/pdf-1863.pdf<\/p>\n

[7] National Haemophilia Foundation for all bleeding disorders-current treatments. https:\/\/www.hemophilia.org\/bleeding-disorders-a-z\/treatment\/current-treatments<\/p>\n

[8]<\/a> World Federation of Haemophilia Guidelines for the Management of Haemophilia. https:\/\/www1.wfh.org\/publications\/files\/pdf-1863.pdf<\/p>\n","protected":false},"excerpt":{"rendered":"

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[2] Mannucci, P., 2020. Hemophilia therapy: the future has begun.Haematologica, 105(3), pp.545-553. 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